Hope for Rare Diseases
The Glycosylation Flux Enhancer Project
When a child is diagnosed with a rare disease and no treatment exists, families are left with devastating uncertainty. At Sanford Burnham Prebys, we’re working to change that.
Led by Dr. Hudson Freeze, our team is launching an innovative program focused on childhood rare diseases, starting with CDG (Congenital Disorders of Glycosylation), a life-threatening condition with no cure.
By combining stem cell science, AI, and drug repurposing, we’re uncovering potential treatments faster, using safe, existing FDA-approved medicines.
Now is the moment to act. A generous donor, T. Denny Sanford, will match every gift, doubling your impact up to $750,000. Your support fuels expert scientists, early-career researchers, and life-saving discoveries.
Science + Speed + Smart Repurposing = Real Hope
If you have any questions, please contact us at (858) 795-5070 or email giving@sbpdiscovery.org.